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Mucopolysaccharidosis III

Showing 1 - 25 of 9,854

STUDY
CONDITIONS
INTERVENTIONS
LOCATIONS

Mucopolysaccharidosis III-A Trial in Hamburg (JR-441)

Recruiting
  • Mucopolysaccharidosis III-A
  • Hamburg, Germany
    Universitätsklinikum Hamburg-Eppendorf
Oct 18, 2023

MPS (RaDiCo Cohort) (RaDiCo-MPS)

Recruiting
  • Mucopolysaccharidosis I
  • +7 more
    • Angers, France
    • +22 more
    Sep 12, 2023

    MPS IIIA, Sanfilippo Syndrome, Sanfilippo A Trial in Australia, Spain, United States (ABO-102)

    Active, not recruiting
    • MPS IIIA
    • +3 more
    • ABO-102
    • Columbus, Ohio
    • +4 more
    Nov 8, 2022

    Participants With Sanfilippo Syndrome Type IIIC

    Not yet recruiting
    • Sanfilippo Syndrome Type C
      • Bron, France
        Hospices Civils De Lyon
      Apr 20, 2023

      Mucopolysaccharidosis Type IIIB, MPS III B Trial in Worldwide (AX 250)

      Active, not recruiting
      • Mucopolysaccharidosis Type IIIB
      • MPS III B
      • AX 250
      • Oakland, California
      • +7 more
      Jan 16, 2023

      Study of Patients With MPS IIIA Treated With ABO-102

      Enrolling by invitation
      • Mucopolysaccharidosis III-A
      • ABO-102
      • Columbus, Ohio
      • +2 more
      Nov 8, 2022

      Patients With Sanfilippo Disease(s) (MPS3)

      Not yet recruiting
      • Sanfilippo Syndrome
      • MPS3
        • Fairfax, Virginia
          LDRTC
        Jan 20, 2023

        Study of Patients With MPS IIIB Treated With ABO-101

        Terminated
        • Mucopolysaccharidosis III-B
        • ABO-101
        • Columbus, Ohio
        • +2 more
        May 25, 2022

        Mucopolysaccharidosis Type 3 B Trial in Worldwide (rAAV9.CMV.hNAGLU)

        Terminated
        • Mucopolysaccharidosis Type 3 B
        • rAAV9.CMV.hNAGLU
        • Columbus, Ohio
        • +3 more
        Apr 29, 2022

        A Natural History Study of Sanfilippo Syndrome Type D

        Recruiting
        • Sanfilippo Syndrome Type D
          • New York, New York
            Columbia University Irving Medical Center
          Jan 11, 2023

          Mucopolysaccharidosis II Trial in Worldwide (JR-141, Idursulfase, JR-141 or Idursulfase)

          Recruiting
          • Mucopolysaccharidosis II
          • Oakland, California
          • +8 more
          Dec 2, 2022

          MPS III B Trial in Worldwide (AX 250)

          Not yet recruiting
          • MPS III B
          • AX 250
          • Oakland, California
          • +4 more
          Aug 8, 2022

          ScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn

          Enrolling by invitation
          • Acid Sphingomyelinase Deficiency
          • +13 more
          • Confirmatory Testing
          • Bronx, New York
          • +9 more
          May 9, 2022

          Mucopolysaccharidosis II Trial in Japan (JR-141)

          Completed
          • Mucopolysaccharidosis II
          • Fukui, Japan
          • +18 more
          Nov 10, 2022

          Sanfilippo Syndrome A Trial (assessment)

          Not yet recruiting
          • Sanfilippo Syndrome A
          • assessment
          • (no location specified)
          Jun 6, 2021

          Mucopolysaccharidosis Type IIIA Trial in Worldwide (LYS-SAF302)

          Active, not recruiting
          • Mucopolysaccharidosis Type IIIA
          • Orange, California
          • +7 more
          Aug 30, 2021

          Mucopolysaccharidosis Type IIIA Trial in Manchester (Autologous CD34+ cells transduced with a lentiviral vector containing the

          Active, not recruiting
          • Mucopolysaccharidosis Type IIIA
          • Autologous CD34+ cells transduced with a lentiviral vector containing the human SGSH gene
          • Manchester, United Kingdom
            Manchester University NHS Foundation Trust
          Jul 2, 2021

          Sanfilippo Syndrome Type A (MPS IIIA) Trial in Oakland, Chapel Hill, Ankara (SOBI003)

          Completed
          • Sanfilippo Syndrome Type A (MPS IIIA)
          • Oakland, California
          • +2 more
          Feb 2, 2022

          Mucopolysaccharidosis Type IIIB

          Completed
          • Sanfilippo Syndrome Type B
            • Oakland, California
            • +3 more
            Mar 15, 2021

            A Study of Patients With Sanfilippo Syndrome Type A (MPS IIIA)

            Completed
            • Sanfilippo Syndrome Type A
            • assessment
            • Minneapolis, Minnesota
              University of Minnesota
            May 19, 2021

            Sanfilippo Syndrome Type A (MPS IIIA) Trial in Germany, Turkey, United States (SOBI003)

            Completed
            • Sanfilippo Syndrome Type A (MPS IIIA)
            • Oakland, California
            • +3 more
            Nov 18, 2021

            MPS III B, Mucopolysaccharidosis Type IIIB Trial in Worldwide (AX 250)

            Completed
            • MPS III B
            • Mucopolysaccharidosis Type IIIB
            • AX 250
            • Oakland, California
            • +6 more
            Aug 4, 2020

            Mucopolysaccharidosis II Trial in Worldwide (Iduronate-2-sulfatase enzyme replacement therapy, iduronate-2-sulfatase enzyme

            Completed
            • Mucopolysaccharidosis II
            • Iduronate-2-sulfatase enzyme replacement therapy
            • +2 more
            • Oakland, California
            • +8 more
            May 30, 2021

            A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

            Completed
            • Mucopolysaccharidosis Type IIIB
            • +3 more
              • Oakland, California
              • +7 more
              Mar 4, 2020